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Thérapie génique Glial cells Cell culture model Myostatin Skeletal muscle Antisense oligonucleotides Cell penetrating peptide Mouse models Oligodendrocytes Oligodendrocyte CONGENITAL MYATHENIC SYNDROME Glucocorticoid-receptor CRISPRi Cell model Dystrophie myotonique Myotonic Dystrophy Type 1 Brain dysfunction PacBio Myelin Acute coronary syndrome Glutamate Gene editing RNA biology Quantitative microdialysis Astrocyte GSK3␤ RNA interference CTG repeats Desmin Transcriptomics Dystrophie Myotonique DMSXL mice In vivo Intermediate filament Glucocorticoids Transgenic mouse AAV KNOCKOUT MICE Acetylcholinesterase knockout mouse Gene Therapy Brain Exercice Central nervous system DMPK Exercise Endurance training ARN Myotonic dystrophy mouse models Acetylcholinesterase deficiency Motoneuron Expression Long read sequencing Dynamin 2 Knockout Mouse model Mice CTG repeat instability PCR BIOLOGIE MOLECULAIRE Neuron Gene therapy Myotonic Dystrophy Muscle Male Myotonic dystrophy type 1 Trinucleotide Repeat Expansion Heart failure RNA splicing Animals Therapy Heart Humans Antisense oligonucleotide Maximal force CMS Myotonic dystrophy Aging Dystrophin Alternative splicing Cytoskeleton Fibrosis MBNL Duchenne muscular dystrophy ACETYLCHOLINESTERASE Dilated cardiomyopathy Autophagy CRISPR/Cas9 Cardiac muscle DM1 GABA Myotonic Dystrophy type 1 Transgenic mouse model CTG repeat contractions Muscular dystrophy Hypoxia Diaphragm Genotype phenotype correlation Astrocytes Trinucleotide repeat expansion Centronuclear myopathy