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Dilated cardiomyopathy Cell culture model Dynamin 2 PCR Myotonic dystrophy BIOLOGIE MOLECULAIRE Myostatin Mouse model Muscle Astrocyte In vivo Oligodendrocyte Intermediate filament Transcriptomics Humans Acute coronary syndrome Male MBNL Aging CMS Acetylcholinesterase deficiency KNOCKOUT MICE Dystrophie myotonique CTG repeat contractions Antisense oligonucleotides Transgenic mouse Lc3 Myotonic dystrophy type 1 Myelin Cell model Alternative splicing Muscular dystrophy Transgenic mouse model CRISPR/Cas9 Oligodendrocytes Brain ARN Motoneuron CTG repeats Knockout Thérapie génique Animals Glucocorticoid-receptor Genotype phenotype correlation RNA interference Gene therapy RNA biology CONGENITAL MYATHENIC SYNDROME ACETYLCHOLINESTERASE Long read sequencing CRISPRi Myotonic dystrophy mouse models Hypoxia Autophagy DMSXL mice Duchenne muscular dystrophy Cytoskeleton Central nervous system Brain dysfunction Trinucleotide Repeat Expansion GSK3␤ Gene Therapy Heart failure Cell penetrating peptide DM1 Quantitative microdialysis Cardiac muscle Maximal force Glutamate Trinucleotide repeat expansion Antisense oligonucleotide Glial cells Diaphragm Exercise Dystrophin Desmin Gene editing GABA Skeletal muscle Exercice Therapy DMPK Mice Myotonic Dystrophy Myotonic Dystrophy Type 1 Fibrosis Neuron Acetylcholinesterase knockout mouse Myotonic Dystrophy type 1 RNA splicing Mouse models Centronuclear myopathy Dystrophie Myotonique PacBio Heart Expression CTG repeat instability AAV Astrocytes Glucocorticoids